I think that would be very important to give regulators those tools to say, 'You have explored this.'
The Cure America Act, I think, was terrific.
The bipartisan OPEN ACT, S. 1509, introduced by Senators Hatch and Menendez, is a patient-driven solution.
If nothing happens, then I am disappointed.
The power of the patient in moving studies forward cannot be understated.
Are we able to watch another video? Do you want to introduce it, Dr. Strupp?
I want to thank you all for testifying, for coming and taking your time.
But are they going to be an acceptable part of your presentation, do you think, to the F.D.A.?
I think something needs to be done to the Orphan Drug Act to actually maybe separate a category or have a separate pathw...
Quality of life should be the key.
I think, we are maybe, the pendulum is over here, and it needs to come back toward the middle.