05/03/2010
https://www.congress.gov...
"This committee has shown great leadership on this issue in the past, and I am committed to seeing it continue to ensure progress continues for children with rare and neglected diseases."
"That is why Senator Specter and I introduced Nino's Act, S. 406, which will allow children to transition out of successful treatment in NIH studies without a gap in treatment."
"One challenge that many of the witnesses today spoke of is the need to incentivize the device and drug/biotech industry to develop therapeutics for rare, pediatric diseases."
"How many of these are rare diseases? Is there any effort underway to expand the number of diseases we screen for? Why or why not?"